Baliforsen sodium |
Catalog No.GC70939 |
Baliforsen sodium es un oligonucleótido antisentido 16 nucleótidos diseñados para atacar la distrofia miotónica proteína quinasa DMPK ARNm y la distrofia miotónica de investigación.
Products are for research use only. Not for human use. We do not sell to patients.
Cas No.: 1687746-79-7
Sample solution is provided at 25 µL, 10mM.
Baliforsen (sodium) is an antisense oligonucleotide (16 nucleotides) designed to target myotonic dystrophy protein kinase (DMPK) mRNA and research myotonic dystrophy.
References:
[1]. Wheeler TM, Leger AJ, Pandey SK, et al. Targeting nuclear RNA for in vivo correction of myotonic dystrophy. Nature. 2012;488(7409):111-115.
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